Development of a novel oral treatment that rescues gait ataxia and retinal degeneration in a phenotypic mouse model of familial dysautonomia. https://www.biorxiv.org/content/10.1101/2022.11.04.515198
Development of a novel oral treatment that rescues gait ataxia and retinal degeneration in a phenotypic mouse model of familial dysautonomia. https://www.biorxiv.org/content/10.1101/2022.11.04.515198