Efficient delivery of FMR1 across the blood brain barrier using 2 AAVphp construct in adult FMR1 KO mice demonstrates the 3 feasibility of gene therapy for fragile X syndrome https://www.biorxiv.org/content/10.1101/2022.12.22.520936v1?med=mas
Efficient delivery of FMR1 across the blood brain barrier using 2 AAVphp construct in adult FMR1 KO mice demonstrates the 3 feasibility of gene therapy for fragile X syndrome https://www.biorxiv.org/content/10.1101/2022.12.22.520936v1?med=mas