Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing https://www.biorxiv.org/content/10.1101/2023.04.06.535786v1?med=mas
Therapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing https://www.biorxiv.org/content/10.1101/2023.04.06.535786v1?med=mas