Gene therapy using optimized LentiHBBT87Q vector in two patients with transfusion dependent β-thalassemia https://www.medrxiv.org/content/10.1101/2023.03.21.23287513
Gene therapy using optimized LentiHBBT87Q vector in two patients with transfusion dependent β-thalassemia https://www.medrxiv.org/content/10.1101/2023.03.21.23287513